Overview
Since November 2004, Charley’s Fund has directed $18 million into medical research to expedite the development of treatments for Duchenne muscular dystrophy. Initially our focus was translational research – research that moves the science from the laboratory into human clinical trials. We are pleased to report that we are now also funding clinical research. This is a clear indication that hopeful therapies are moving through the drug development pipeline. Through innovative partnerships with biotechnology companies and clinicians, we are having a clear and measurable impact on the speed of drug development for Duchenne muscular dystrophy. For further details, please click on each therapeutic strategy.
Sarepta Therpaeutics
Charley’s Fund has partnered with Sarepta Therpaeutics to optimize the company’s backbone chemistry ...
Halo Therapeutics
Halo Therapeutics was founded to acquire and develop a powerful anti-fibrotic drug ...
PTC Therapeutics
This NJ-based biotech company is developing oral medications that may delay muscle ...
Retrophin
Retrophin is an emerging biotechnology company focused on rare and life-threatening diseases. ...
Pilot Trials Now
Pilot Trials Now is a collaboration between several nonprofit foundations including Charley’s ...
Convergence Medical Devices
CMD was formed to optimize and develop an incredible technological advancement discovered ...







